Gene Therapy Research for #SMA!!!

E take a minute to read how gene therapy is reversing the effects of Spinal Muscular Atrophy (SMA) in mice models. We are SO close to curing SMA!!! Praying for a cure.....
COLUMBUS, Ohio – Reversing a protein deficiency through gene therapy can correct motor function, restore nerve signals and improve survival in mice that serve as a model for the lethal childhood disorderspinal muscular atrophy, new research shows.

Within 13 days after the injection, 90 percent of the treated mice had the muscle coordination needed to right themselves as quickly as normal animals. By this time, untreated SMA mice already were suffering symptoms that left them unable to right themselves. The day-1 treated mice also were nearly identical to normal mice in their ability to run on a wheel.


Nancy Lee said…
Wow! I knew they were close, but I didn't know they were this close. That is exciting!